paternal uniparental disomy of chromosome 1

ORPHA: 251004

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with paternal uniparental disomy of chromosome 1, sourced from HPO and Orphanet clinical annotations.

ProteinuriaEnlarged kidneyStrabismusProgressive visual lossPhotophobiaAbnormal dental enamel morphologyMembranoproliferative glomerulonephritisHypertensionDelayed pubertyAnhidrosisSeizureNeonatal hypotoniaMyoclonusCraniosynostosisObesityPolyphagiaRecurrent fracturesHypercalcemiaIncreased blood urea nitrogenShort statureEpisodic hemolytic anemiaPain insensitivityProgressive psychomotor deteriorationDyschromatopsiaMacular dystrophyAbnormal blistering of the skinBrain atrophyMacroscopic hematuriaAbnormal retinal morphology on macular OCT

Classification & Codes

Orphanet Code

ORPHA:251004
paternal uniparental disomy of chromosome 1
OrphanetORPHA:251004
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO