PCNA-related progressive neurodegenerative photosensitivy syndrome

ORPHA: 438134

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with PCNA-related progressive neurodegenerative photosensitivy syndrome, sourced from HPO and Orphanet clinical annotations.

Hearing impairmentPhotophobiaCutaneous photosensitivityGlobal developmental delayGait ataxiaNeurodegenerationTelangiectasia of the skinMild intellectual disabilityShort statureRetinal telangiectasiaAbsent pubertal growth spurtMicrocephalyCongenital diaphragmatic herniaCerebellar atrophyNeoplasmSevere intellectual disability

Classification & Codes

Orphanet Code

ORPHA:438134
PCNA-related progressive neurodegenerative photosensitivy syndrome
OrphanetORPHA:438134
Treatments0 drug(s)
Symptoms on record16 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
PCNA-related progressive neurodegenerative photosensitivy syndrome | OrphanDrug