PHGDH deficiency, infantile/juvenile form

MeSH: C566618ORPHA: 79351

Overview

serine deficiency that has material basis in deficiency of phosphoglycerate dehydrogenase which results in a disruption of L-serine biosynthesis

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with PHGDH deficiency, infantile/juvenile form, sourced from HPO and Orphanet clinical annotations.

Cerebral hypoplasiaHypoglycinemiaHyposerinemiaMicrocephalyEsotropiaSpasticityFailure to thriveIntrauterine growth retardationVomitingShort statureCerebral hypomyelinationDevelopmental stagnationEpileptic spasmSevere global developmental delayPrimary microcephalyFeeding difficultiesDelayed myelinationCerebral white matter atrophyInguinal herniaHypogonadismDevelopmental cataractAtypical behaviorIrritabilityAdducted thumbHypertoniaUmbilical herniaMegaloblastic anemiaAbnormal facial shapeGastroesophageal refluxBilateral tonic-clonic seizureHypoplasia of the corpus callosumVentriculomegalyGeneralized non-motor (absence) seizureGeneralized myoclonic seizureAthetosisSpastic tetraplegiaAbnormal cortical gyrationGeneralized ichthyosisAbnormality of hair textureAtonic seizureFocal emotional seizure with laughingModerate global developmental delayInappropriate cryingEsophagitisCerebral visual impairment

Classification & Codes

MeSH Code

C566618

Orphanet Code

ORPHA:79351
PHGDH deficiency, infantile/juvenile form
MeSHC566618
OrphanetORPHA:79351
Treatments0 drug(s)
Symptoms on record45 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO