Phosphoenolpyruvate carboxykinase deficiency, mitochondrial

MeSH: C564890ORPHA: 79317

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C564890

Orphanet Code

ORPHA:79317
Phosphoenolpyruvate carboxykinase deficiency, mitochondrial
MeSHC564890
OrphanetORPHA:79317
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO