phosphofructokinase deficiency

MeSH: D006014ORPHA: 371

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with phosphofructokinase deficiency, sourced from HPO and Orphanet clinical annotations.

Muscle weaknessAnemiaHyperuricemiaMyotoniaSkeletal muscle atrophyIncreased muscle glycogen content

Classification & Codes

MeSH Code

D006014

Orphanet Code

ORPHA:371
phosphofructokinase deficiency
MeSHD006014
OrphanetORPHA:371
Treatments0 drug(s)
Symptoms on record6 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO