phosphoribosylpyrophosphate synthetase superactivity

MeSH: C567064ORPHA: 3222

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with phosphoribosylpyrophosphate synthetase superactivity, sourced from HPO and Orphanet clinical annotations.

Sensorineural hearing impairmentAtaxiaHyperuricemiaRenal insufficiencyIntellectual disabilityHypotoniaAbnormal aortic morphologyAbnormal speech patternStrabismusAbnormality of eye movementHypertensionCardiomyopathyArrhythmia

Classification & Codes

MeSH Code

C567064

Orphanet Code

ORPHA:3222
phosphoribosylpyrophosphate synthetase superactivity
MeSHC567064
OrphanetORPHA:3222
Treatments0 drug(s)
Symptoms on record13 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO