polyostotic fibrous dysplasia

MeSH: D005359ORPHA: 932762 Treatments Available

Overview

autosomal dominant disease that involves skin pigmentation, bone and hormonal problems along with premature puberty

Available Treatments (2)

DrugFormStatusCountriesLead Time
Denosumab
Cold Chain
Subcutaneous injection, 120mg/1.7mL solutionFDA Approved714d
Pamidronate
IV infusion, 30mg, 60mg, 90mg powder for reconstitutionFDA Approved107d

Classification & Codes

MeSH Code

D005359

Orphanet Code

ORPHA:93276
polyostotic fibrous dysplasia
MeSHD005359
OrphanetORPHA:93276
Treatments2 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO