pretibial dystrophic epidermolysis bullosa

MeSH: C535494ORPHA: 794101 Treatment Available

Overview

Pretibial dystrophic epidermolysis bullosa is a rare subtype of dystrophic epidermolysis bullosa (DEB, see this term) characterized by the development of blisters, erosions, and lichenoid lesions predominantly in the pretibial region

Available Treatments (1)

DrugFormStatusCountriesLead Time
Beremagene geperpavec
Orphan Cold Chain
Topical gel, 1×10^7 PFU/cm²FDA Approved114d

Clinical Presentation

Signs and symptoms associated with pretibial dystrophic epidermolysis bullosa, sourced from HPO and Orphanet clinical annotations.

Abnormal blistering of the skinLocalized skin lesionPretibial blisteringAtypical scarring of skinPruritusFragile skinMiliaAtrophic scarsAbnormal fingernail morphologyAnonychiaPalmoplantar blisteringAbnormal toenail morphologyNail dystrophyKeloidsAbnormality of the eyeCarious teethSmall nailMitten deformityErythematous papuleHyperkeratotic papuleSkin vesicleSkin erosionOral mucosal blisters

Classification & Codes

MeSH Code

C535494

Orphanet Code

ORPHA:79410
pretibial dystrophic epidermolysis bullosa
MeSHC535494
OrphanetORPHA:79410
Treatments1 drug(s)
Symptoms on record23 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
pretibial dystrophic epidermolysis bullosa | OrphanDrug