primary localized amyloidosis
ORPHA: 3147091 Treatment Available
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Patisiran Orphan Cold Chain | IV infusion, 2 mg/mL | FDA Approved | 6 | — |
Classification & Codes
Orphanet Code
ORPHA:314709primary localized amyloidosis
| Orphanet | ORPHA:314709 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO