properdin deficiency

MeSH: C537241ORPHA: 29661 Treatment Available

Overview

human disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
eculizumab
Orphan Cold Chain
IV infusion, 10mg/mL concentrate for solutionFDA Approved, EMA Approved914d

Classification & Codes

MeSH Code

C537241

Orphanet Code

ORPHA:2966
properdin deficiency
MeSHC537241
OrphanetORPHA:2966
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO