proximal myopathy with extrapyramidal signs

ORPHA: 401768

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with proximal myopathy with extrapyramidal signs, sourced from HPO and Orphanet clinical annotations.

Global developmental delayGait disturbanceDystoniaChoreaOrofacial dyskinesiaResting tremorIncreased variability in muscle fiber diameterCentrally nucleated skeletal muscle fibersProximal muscle weaknessInvoluntary movementsProgressive extrapyramidal movement disorderProgressive extrapyramidal muscular rigidityDifficulty runningAbnormal basal ganglia MRI signal intensityCentral core regions in muscle fibersMicrocephalyPtosisOphthalmoplegiaOptic atrophyAtaxiaPeripheral axonal neuropathyMildly elevated creatine kinase

Classification & Codes

Orphanet Code

ORPHA:401768
proximal myopathy with extrapyramidal signs
OrphanetORPHA:401768
Treatments0 drug(s)
Symptoms on record22 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO