PrP systemic amyloidosis

ORPHA: 397606

Overview

(20p13) leading to deposition of prion protein amyloid

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

Orphanet Code

ORPHA:397606
PrP systemic amyloidosis
OrphanetORPHA:397606
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO