pyridoxal phosphate-responsive seizures

MeSH: C566449ORPHA: 79096

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with pyridoxal phosphate-responsive seizures, sourced from HPO and Orphanet clinical annotations.

Status epilepticusEpileptic encephalopathyAbnormality of eye movementSeizureGlobal developmental delayHypertoniaMyoclonusFailure to thriveAbnormality of the amniotic fluidPremature birthMetabolic acidosisHypoglycemiaIncreased circulating lactate concentrationGlobal brain atrophyUnsteady gaitDecreased CSF homovanillic acid concentrationHypoargininemiaAxial hypotoniaEEG with burst suppressionFeeding difficultiesHigh-pitched cryLow APGAR scoreMicrocephalyPyridoxine-responsive sideroblastic anemiaAbnormal circulating glycine concentrationAbnormal circulating threonine concentrationAbnormal circulating histidine concentrationAbnormal circulating arginine concentrationAbnormal circulating tyrosine concentration

Classification & Codes

MeSH Code

C566449

Orphanet Code

ORPHA:79096
pyridoxal phosphate-responsive seizures
MeSHC566449
OrphanetORPHA:79096
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO