rare genetic skin disease

ORPHA: 683463 Treatments Available

Overview

human disease

Available Treatments (3)

DrugFormStatusCountriesLead Time
Bimekizumab-bkzx
Cold Chain
Subcutaneous injectionFDA Approved37d
Palovarotene
Orphan
CapsuleFDA Approved114d
Calcipotriol
Cream, Ointment, SolutionApproved45d

Classification & Codes

Orphanet Code

ORPHA:68346
rare genetic skin disease
OrphanetORPHA:68346
Treatments3 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO