severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, Nk cell-positive

ORPHA: 331206

Overview

severe combined immunodeficiency characterized by being T cell-negative, B cell-negative and natural killer cell-positive and that has material basis in mutation in the RAG1 and RAG2 genes on chromosome 11p12

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, Nk cell-positive, sourced from HPO and Orphanet clinical annotations.

Decreased circulating IgA concentrationDecreased circulating total IgMDecreased circulating immunoglobulin concentrationDecreased circulating IgG concentrationRecurrent viral infectionsAbnormal B cell countAbnormal total T cell countFailure to thriveDecreased total lymphocyte countFeverRecurrent bacterial infectionsRecurrent enteroviral infectionsRecurrent fungal infectionsProtracted diarrheaDecreased mitogen-induced T-cell proliferationReduced antigen-specific T cell proliferationDecreased total T cell countRecurrent upper and lower respiratory tract infectionsPallorSkin rashHepatosplenomegalyThrombocytopeniaIncreased total eosinophil countAutoimmune hemolytic anemiaHepatomegalyLymphadenitisElevated circulating hepatic transaminase concentrationAutoimmunityAbnormal total natural killer cell count

Classification & Codes

Orphanet Code

ORPHA:331206
severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, Nk cell-positive
OrphanetORPHA:331206
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO