spastic tetraplegia-retinitis pigmentosa-intellectual disability syndrome

MeSH: C564808ORPHA: 3011

Overview

Spastic tetraplegia-retinitis pigmentosa-intellectual disability syndrome is characterized by nonprogressive spastic paraplegia, retinitis pigmentosa, and intellectual deficit. It has been described in two brothers born to consanguineous parents.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with spastic tetraplegia-retinitis pigmentosa-intellectual disability syndrome, sourced from HPO and Orphanet clinical annotations.

Rod-cone dystrophySeverely reduced visual acuityProfound intellectual disabilityDevelopmental regressionInfantile sensorineural hearing impairment

Classification & Codes

MeSH Code

C564808

Orphanet Code

ORPHA:3011
spastic tetraplegia-retinitis pigmentosa-intellectual disability syndrome
MeSHC564808
OrphanetORPHA:3011
Treatments0 drug(s)
Symptoms on record5 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO