syndrome with corpus callosum agenesis /dysgenesis as a major feature

ORPHA: 1996392 Treatments Available

Overview

human disease

Available Treatments (2)

DrugFormStatusCountriesLead Time
Vigabatrin
Orphan
Oral tablet 500mg; Oral powder for solution 500mg sachetsFDA Approved, EMA Approved614d
Levetiracetam
Oral tablet 250mg, 500mg, 750mg, 1000mg; Oral solution 100mg/mL; IV infusion 500mg/5mLFDA Approved, EMA Approved113d

Classification & Codes

Orphanet Code

ORPHA:199639
syndrome with corpus callosum agenesis /dysgenesis as a major feature
OrphanetORPHA:199639
Treatments2 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO