syndromic agammaglobulinemia

ORPHA: 2297201 Treatment Available

Overview

agammaglobulinemia that is part of a larger syndrome

Available Treatments (1)

DrugFormStatusCountriesLead Time
Intravenous Immunoglobulin (IVIG)
Orphan Cold Chain
IV InfusionFDA Approved5

Classification & Codes

Orphanet Code

ORPHA:229720
syndromic agammaglobulinemia
OrphanetORPHA:229720
Treatments1 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO