Tay-Sachs disease AB variant

MeSH: D049290ORPHA: 309246

Overview

extremely rare, severe genetic disorder characterized by progressive neurological decline due to ganglioside activator deficiency

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Tay-Sachs disease AB variant, sourced from HPO and Orphanet clinical annotations.

DystoniaHyperreflexiaCerebral atrophyNeurodegenerationExaggerated startle responseDevelopmental regressionProgressive spastic quadriplegiaShort statureAbnormal pyramidal signAxial hypotoniaHyperacusisCognitive impairmentAbnormal fear-induced behaviorInappropriate behaviorAnxietySeizureChoreaLoss of speechPrimitive reflexPostnatal growth retardationCherry red spot of the maculaAbnormal involuntary eye movementsGlabellar reflexPseudobulbar signsPunctate periventricular T2 hyperintense foci

Classification & Codes

MeSH Code

D049290

Orphanet Code

ORPHA:309246
Tay-Sachs disease AB variant
MeSHD049290
OrphanetORPHA:309246
Treatments0 drug(s)
Symptoms on record25 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO