ventriculomegaly-cystic kidney disease

ORPHA: 4439881 Treatment Available

Overview

human disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
eculizumab
Orphan Cold Chain
IV infusion, 10mg/mL concentrate for solutionFDA Approved, EMA Approved914d

Classification & Codes

Orphanet Code

ORPHA:443988
ventriculomegaly-cystic kidney disease
OrphanetORPHA:443988
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
ventriculomegaly-cystic kidney disease | OrphanDrug