Vici syndrome

MeSH: C535566ORPHA: 1493

Overview

autosomal recessive disease characterized by callosal agenesis, cataracts, cardiomyopathy, combined immunodeficiency and hypopigmentation, with material basis in mutation in the EPG5 gene on chromosome 18q12.3.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Vici syndrome, sourced from HPO and Orphanet clinical annotations.

Hypopigmentation of the skinIntellectual disabilityHypotoniaGlobal developmental delayAgenesis of corpus callosumCardiomyopathyRecurrent respiratory infectionsEEG abnormalityRecurrent infectionsShort statureCellular immunodeficiencyUreteral atresiaAbnormal retinal pigmentationHigh palateDepressed nasal tipCataractNystagmusOptic atrophySeizureCerebellar hypoplasiaRenal tubular acidosisGray matter heterotopiaHypoplasia of the ponsHypertelorismSensorineural hearing impairmentHypotelorismAbnormal macular morphologyJoint stiffnessCerebral cortical atrophySleep disturbanceDecreased circulating IgG concentrationDecreased circulating IgG2 concentrationFeeding difficulties in infancyFeeding difficulties

Classification & Codes

MeSH Code

C535566

Orphanet Code

ORPHA:1493
Vici syndrome
MeSHC535566
OrphanetORPHA:1493
Treatments0 drug(s)
Symptoms on record34 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO