Wolfram Syndrome

ICD-10: 5A52MeSH: D014929ORPHA: 3463

Overview

A progressive neurodegenerative disorder characterized by diabetes insipidus, diabetes mellitus, optic atrophy, and deafness (DIDMOAD). Caused by mutations in the WFS1 gene. Disease prevalence is approximately 1 in 500,000 individuals.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Wolfram Syndrome, sourced from HPO and Orphanet clinical annotations.

Sensorineural hearing impairmentOptic atrophyDiabetes mellitusDiabetes insipidusPolydipsiaRecurrent urinary tract infectionsAbnormality of the urinary systemNephropathyNystagmusSeizureAtaxiaDysarthriaFeeding difficulties in infancyAbnormal mesentery morphologyDysuriaMale hypogonadismHypogonadismGlaucomaOphthalmoplegiaAtypical behaviorDementiaHallucinationsDelayed pubertyIntellectual disabilityJoint stiffnessCardiomyopathyAnemiaConstipationMalabsorptionRespiratory insufficiencyCerebral cortical atrophyGastrointestinal hemorrhageSleep disturbanceDevelopmental regressionGastric ulcerCentral apneaMyopathyPeripheral neuropathyAbnormal autonomic nervous system physiology

Classification & Codes

ICD-10 Code

5A52

MeSH Code

D014929

Orphanet Code

ORPHA:3463
Wolfram Syndrome
ICD-105A52
MeSHD014929
OrphanetORPHA:3463
Treatments0 drug(s)
Symptoms on record39 signs
Statuspublished
Factual Authority
Last Updated3/21/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO