X-linked adrenal hypoplasia congenita

ORPHA: 95702

Overview

adrenal cortical hypofunction that is characterized by a reduction in adrenal gland function resulting from incomplete development of the adrenal cortex and has material basis in the nuclear receptor NR0B1 (DAX1) gene

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with X-linked adrenal hypoplasia congenita, sourced from HPO and Orphanet clinical annotations.

Decreased serum testosterone concentrationDecreased libidoErectile dysfunctionSeizureWeight lossSparse pubic hairIncreased circulating ACTH levelHyperpigmentation of the skinDecreased circulating cortisol levelHypogonadotropic hypogonadismOligozoospermiaDelayed pubertyFailure to thrive in infancyVomitingDiarrheaNauseaHyperkalemiaVertigoHyponatremiaAdrenocortical cytomegalyPrimary adrenal insufficiencyDecreased testicular sizeFatigueDecreased circulating luteinizing hormone level

Classification & Codes

Orphanet Code

ORPHA:95702
X-linked adrenal hypoplasia congenita
OrphanetORPHA:95702
Treatments0 drug(s)
Symptoms on record24 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO