X-linked distal spinal muscular atrophy type 3

MeSH: C564506ORPHA: 139557

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C564506

Orphanet Code

ORPHA:139557
X-linked distal spinal muscular atrophy type 3
MeSHC564506
OrphanetORPHA:139557
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO