X-linked distal spinal muscular atrophy type 3
MeSH: C564506ORPHA: 139557
Overview
human disease
Available Treatments (0)
No treatments linked yet
Clinical trials or compassionate use may be available — consult a specialist.
Classification & Codes
MeSH Code
C564506Orphanet Code
ORPHA:139557X-linked distal spinal muscular atrophy type 3
| MeSH | C564506 |
| Orphanet | ORPHA:139557 |
| Treatments | 0 drug(s) |
| Status | published |
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO