X-linked intellectual disability-cerebellar hypoplasia-spondylo-epiphyseal dysplasia syndrome

ORPHA: 459070

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with X-linked intellectual disability-cerebellar hypoplasia-spondylo-epiphyseal dysplasia syndrome, sourced from HPO and Orphanet clinical annotations.

SeizureAbnormal facial shapeSevere intellectual disabilityCryptorchidismMicrocephalyMandibular prognathiaMacrotiaAutismDelayed speech and language developmentAtaxiaCerebellar hypoplasiaAbsent speechGrowth delayGastroesophageal refluxScoliosisSpondyloepiphyseal dysplasiaFloppy infantAnteverted earsInguinal herniaHypospadiasNarrow mouthThin upper lip vermilionEverted lower lip vermilionDolichocephalyLong faceEpicanthusMicroretrognathiaSmooth philtrumBroad foreheadLong philtrumLow-set earsSensorineural hearing impairmentProtruding earRod-cone dystrophyMyopiaExotropiaDelayed pubertyOsteoporosisSingle transverse palmar creaseSacral dimpleHirsutismTapered fingerPolyhydramniosLaryngomalaciaVentricular septal defectAtrial septal defectToe syndactylyBilateral tonic-clonic seizureFebrile seizure (within the age range of 3 months to 6 years)Inability to walkRecurrent infectionsClinodactyly of the 5th fingerPulmonary artery stenosisLower-limb joint contractureDilatation of the ventricular cavityFocal-onset seizureDecreased testicular sizeShort fingerGeneralized tonic seizureLipomaWide nasal ridgeIncreased theta frequency activity in EEGNarrow palpebral fissure

Classification & Codes

Orphanet Code

ORPHA:459070
X-linked intellectual disability-cerebellar hypoplasia-spondylo-epiphyseal dysplasia syndrome
OrphanetORPHA:459070
Treatments0 drug(s)
Symptoms on record63 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO