asciminib

Orphan DrugFDA Approved, EMA Approved

Description

Asciminib is the first specifically targeting ABL myristoyl pocket (STAMP) inhibitor. It provides a new mechanism of action for treating chronic myeloid leukemia, particularly beneficial for patients who have developed resistance to previous TKI therapies.

Indications & Therapeutic Use

Philadelphia chromosome-positive chronic myeloid leukemia

Linked Diseases:

Global Availability (4 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
asciminib
Generic Nameasciminib
Brands1 brand available
Active Ingredientasciminib hydrochloride
Drug ClassPhiladelphia chromosome-positive chronic myeloid leukemia
ManufacturerNovartis
Dosage FormsOral tablets, 20mg and 40mg
Medical CodeL01EA04
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Lead Time7 days
Reg. StatusFDA Approved, EMA Approved
Clinical TrialNCT02081378
Countries4 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations5 Validated Nodes