mannose-1-phosphate

Orphan Drug Cold Chain RequiredInvestigational

Description

Mannose-1-phosphate is an investigational therapy for congenital disorders of glycosylation (CDG), specifically targeting MPI-CDG (CDG-Ib). It aims to bypass the enzymatic defect by providing the missing substrate for proper glycosylation. Clinical trials are ongoing to evaluate safety and efficacy in patients with CDG type II disorders.

Indications & Therapeutic Use

congenital disorders of glycosylation type II

Global Availability (4 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
mannose-1-phosphate
Generic Namemannose-1-phosphate
Active Ingredientmannose-1-phosphate
Drug Classcongenital disorders of glycosylation type II
Dosage FormsIV infusion (investigational)
Orphan StatusYes — Orphan Drug
Cold ChainRequired
Lead Time30 days
Reg. StatusInvestigational
Clinical TrialNCT02955264
Countries4 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations5 Validated Nodes