Vorasidenib

Orphan DrugFDA Approved

Description

Vorasidenib is an oral inhibitor of mutant isocitrate dehydrogenase-1 and 2 (IDH1/2) enzymes. It is indicated for adult patients with IDH1- or IDH2-mutant low-grade glioma.

Indications & Therapeutic Use

Low-grade glioma

Linked Diseases:

Global Availability (1 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Vorasidenib
Generic NameVorasidenib
Brands1 brand available
Active IngredientVorasidenib
Drug ClassLow-grade glioma
ManufacturerServier Pharmaceuticals
Dosage FormsTablet
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Lead Time14 days
Reg. StatusFDA Approved
Clinical TrialNCT04164901
Countries1 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations2 Validated Nodes