Orphan Drugs — E | OrphanDrug

eculizumab

Orphan Cold Chain14dFDA Approved, EMA Approved

Edaravone

Orphan7dFDA Approved

efgartigimod alfa

Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022), Japan Approved (2022)

eladocagene exuparvovec

Orphan Cold Chain45dEMA Approved (2022)

eliglustat

Orphan10dFDA Approved, EMA Approved

eplontersen

Orphan Cold Chain21dFDA Approved (2023), EMA Approved (2024)

Epoprostenol

Orphan Cold Chain14dFDA Approved

eribulin mesylate

Orphan Cold Chain14dFDA Approved

Erythropoietin

Orphan Cold Chain14dFDA Approved

Eteplirsen

Orphan Cold ChainFDA Approved

Everolimus

OrphanFDA Approved

Orphan & Rare Drug Database