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OrphanDrug
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

11 entries
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Orphan Drugs Only
eculizumab
Orphan Cold Chain14dFDA Approved, EMA Approved
Edaravone
Orphan7dFDA Approved
efgartigimod alfa
Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022), Japan Approved (2022)
eladocagene exuparvovec
Orphan Cold Chain45dEMA Approved (2022)
eliglustat
Orphan10dFDA Approved, EMA Approved
eplontersen
Orphan Cold Chain21dFDA Approved (2023), EMA Approved (2024)
Epoprostenol
Orphan Cold Chain14dFDA Approved
eribulin mesylate
Orphan Cold Chain14dFDA Approved
Erythropoietin
Orphan Cold Chain14dFDA Approved
Eteplirsen
Orphan Cold ChainFDA Approved
Everolimus
OrphanFDA Approved
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