Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan Drugs Only
Sacrosidase
Orphan
FDA Approved
selumetinib
Orphan
14d
FDA Approved, EMA Approved
sirolimus
Orphan
5d
FDA Approved, EMA Approved
Sodium Phenylbutyrate
Orphan
FDA Approved
Somatrogon-ghla
Orphan
Cold Chain
FDA Approved
Somatropin
Orphan
Cold Chain
14d
FDA Approved