blepharoptosis-myopia-ectopia lentis syndrome

MeSH: C536236ORPHA: 12592 Treatments Available

Overview

This syndrome is characterised by bilateral congenital blepharoptosis, ectopia lentis and high myopia

Available Treatments (2)

DrugFormStatusCountriesLead Time
Acetazolamide
Oral tablets 125mg, 250mg; Injectable powder for reconstitution 500mgFDA Approved112d
botulinum toxin type A
Cold Chain
powder for injection 50 units, 100 units, 200 units per vialFDA Approved914d

Clinical Presentation

Signs and symptoms associated with blepharoptosis-myopia-ectopia lentis syndrome, sourced from HPO and Orphanet clinical annotations.

Prominent occiputGlaucomaPtosisMyopiaIris colobomaEctopia lentisAbnormal retinal pigmentationAbnormal helix morphologyPalpebral edemaFingernail dysplasia

Classification & Codes

MeSH Code

C536236

Orphanet Code

ORPHA:1259
blepharoptosis-myopia-ectopia lentis syndrome
MeSHC536236
OrphanetORPHA:1259
Treatments2 drug(s)
Symptoms on record10 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO