inherited acute myeloid leukemia

ORPHA: 3194652 Treatments Available

Overview

instance of acute myeloid leukemia that is caused by an inherited modification of the individual's genome

Available Treatments (2)

DrugFormStatusCountriesLead Time
cytarabine
Cold Chain
IV infusion, 20mg/mL, 100mg/mL; Intrathecal injection, 50mg/mLFDA Approved, EMA Approved103d
imatinib mesylate
Orphan
Oral tablet, 100mg, 400mgFDA Approved, EMA Approved97d

Classification & Codes

Orphanet Code

ORPHA:319465
inherited acute myeloid leukemia
OrphanetORPHA:319465
Treatments2 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO