Juvenile nephronophthisis

ORPHA: 935921 Treatment Available

Overview

medical condition

Available Treatments (1)

DrugFormStatusCountriesLead Time
Tolvaptan
Orphan
Oral tablet 15mg, 30mg, 45mg, 60mg, 90mgFDA Approved914d

Classification & Codes

Orphanet Code

ORPHA:93592
Juvenile nephronophthisis
OrphanetORPHA:93592
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO