microcephalic osteodysplastic primordial dwarfism type II

MeSH: C565898ORPHA: 26371 Treatment Available

Overview

Human disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
Growth hormone (somatropin)
Orphan Cold Chain
Subcutaneous injection, 5mg, 12mg cartridgesFDA Approved814d

Clinical Presentation

Signs and symptoms associated with microcephalic osteodysplastic primordial dwarfism type II, sourced from HPO and Orphanet clinical annotations.

Abnormal female external genitalia morphologyMicrocephalyRetrognathiaFull cheeksLow-set earsSensorineural hearing impairmentUnderdeveloped nasal alaeWide nasal bridgeProminent noseDownslanted palpebral fissuresMicrodontiaPrecocious pubertyAbnormal metaphysis morphologyDry skinHypopigmented skin patchesBrachydactylyIntellectual disabilitySeizureGlobal developmental delayStrokeIntrauterine growth retardationLaryngomalaciaHypernasal speechAbnormally high-pitched voiceAtrial septal defectPatent ductus arteriosusAnemiaTruncal obesityHypoplasia of the corpus callosumVentriculomegalyRecurrent respiratory infectionsFine hairVascular dilatationScoliosisDelayed skeletal maturationTracheal stenosisCoxa varaHypoplastic iliac wingMicromeliaNarrow pelvis boneDisproportionate short statureClinodactyly of the 5th fingerAbnormal epiphysis morphologyAttention deficit hyperactivity disorderMultiple cafe-au-lait spotsTooth agenesisAplasia/Hypoplasia of the earlobesNarrow palpebral fissureArterial stenosisAbnormal cerebral vascular morphologyAplasia/Hypoplasia of the eyebrowJoint hypermobility

Classification & Codes

MeSH Code

C565898

Orphanet Code

ORPHA:2637
microcephalic osteodysplastic primordial dwarfism type II
MeSHC565898
OrphanetORPHA:2637
Treatments1 drug(s)
Symptoms on record52 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
microcephalic osteodysplastic primordial dwarfism type II | OrphanDrug