oculocutaneous albinism type 6

ORPHA: 3700971 Treatment Available

Overview

disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
Nitisinone
Orphan
Oral capsule, 2mg, 5mg, 10mg, 20mg; Oral suspension, 4mg/mLFDA Approved721d

Clinical Presentation

Signs and symptoms associated with oculocutaneous albinism type 6, sourced from HPO and Orphanet clinical annotations.

PhotophobiaNystagmusAbnormal fundus morphologyReduced visual acuityAbnormal iris pigmentationAplasia/Hypoplasia of the maculaAbnormal foveal morphology on macular OCT

Classification & Codes

Orphanet Code

ORPHA:370097
oculocutaneous albinism type 6
OrphanetORPHA:370097
Treatments1 drug(s)
Symptoms on record7 signs
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO