spondylometaphyseal dysplasia, golden type
MeSH: C563124ORPHA: 1685442 Treatments Available
Overview
human disease
Available Treatments (2)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Growth hormone (somatropin) Orphan Cold Chain | Subcutaneous injection, 5mg, 12mg cartridges | FDA Approved | 8 | 14d |
| Bisphosphonates (pamidronate) | IV infusion 30mg, 60mg, 90mg vials | FDA Approved | 6 | 10d |
Classification & Codes
MeSH Code
C563124Orphanet Code
ORPHA:168544spondylometaphyseal dysplasia, golden type
| MeSH | C563124 |
| Orphanet | ORPHA:168544 |
| Treatments | 2 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO