Xia-Gibbs Syndrome

ORPHA: 4120693 Treatments Available

Overview

autosomal dominant non-syndromic intellectual disability that has material basis in an autosomal dominant mutation of AHDC1 on chromosome 1p36.1-p35.3

Available Treatments (3)

DrugFormStatusCountriesLead Time
Growth hormone (somatropin)
Orphan Cold Chain
Subcutaneous injection, 5mg, 12mg cartridgesFDA Approved814d
Multivitamin with Calcium and Vitamin D
Oral tablets, chewable tablets, liquid suspensionOTC - Multiple jurisdictions91d
Levetiracetam
Oral tablet 250mg, 500mg, 750mg, 1000mg; Oral solution 100mg/mL; IV infusion 500mg/5mLFDA Approved, EMA Approved113d

Clinical Presentation

Signs and symptoms associated with Xia-Gibbs Syndrome, sourced from HPO and Orphanet clinical annotations.

Delayed speech and language developmentIntellectual disabilityHypotoniaGlobal developmental delayMotor delayStrabismusAbnormality of the vertebral columnSeizureAtaxiaAbnormal corpus callosum morphologyJoint hypermobilityFailure to thriveAbnormal facial shapeExpressive language delayUpper airway obstructionObstructive sleep apneaUpbeat nystagmusFeeding difficultiesAbnormal brain morphologyDelayed ability to walkHypertelorismMicrognathiaHearing impairmentLow-set earsSmall earlobeProtruding earDeeply set eyeDownslanted palpebral fissuresEsotropiaUpslanted palpebral fissureAutismCraniosynostosisLaryngomalaciaHypoplasia of the corpus callosumEEG abnormalityScoliosisTracheomalaciaRespiratory failure requiring assisted ventilationDepressed nasal bridgeRetrocerebellar cystUplifted earlobeDelayed myelinationSnoringMild myopiaCerebral visual impairment

Classification & Codes

Orphanet Code

ORPHA:412069
Xia-Gibbs Syndrome
OrphanetORPHA:412069
Treatments3 drug(s)
Symptoms on record45 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO