Cystagon

Orphan DrugFDA Approved

Description

Cystagon is indicated for the treatment of nephropathic cystinosis. It reduces cystine accumulation in cells, leading to delayed progression of renal failure.

Indications & Therapeutic Use

Nephropathic cystinosis

Global Availability (4 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Cystagon
Generic NameCystagon
Brands1 brand available
Active IngredientCysteamine bitartrate
Drug ClassNephropathic cystinosis
ManufacturerMylan
Dosage FormsCapsule
Medical CodeA16AA04
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Reg. StatusFDA Approved
Countries4 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations5 Validated Nodes