AU

Australia

AU

Oceania

Regulatory Overview

Australia is regulated by the TGA (Therapeutic Goods Administration). The country has 2 documented regulatory pathways for accessing unapproved or unlicensed medicines, covering named patient programs, compassionate use schemes, and special access arrangements.

Regulatory Authority

TGA (Therapeutic Goods Administration)

Regulatory Pathways (2)

Allows medical practitioners to supply unapproved therapeutic goods to a class of patients with a particular medical condition without requiring individual TGA approvals for each patient.

Application Form: TGA Authorised Prescriber Application
Legal Basis: Therapeutic Goods Act 1989 Section 19
Eligibility: Serious or life-threatening condition with no locally registered alternative
Reference: TGA Authorised Prescriber Guidance

TGA SAS Category B allows supply of unapproved therapeutic goods to individual patients on a case-by-case basis, with TGA approval required before supply.

Application Form: TGA SAS-B Notification/Approval Form
Legal Basis: Therapeutic Goods Act 1989 Section 19
Eligibility: Serious or life-threatening condition with no locally registered alternative
Reference: TGA SAS Guidelines

Drugs Available (210)

DrugAccess RouteStatusLead Time
alglucosidase alfa
cytarabine
eliglustat
vitamin A (retinol)
furosemide
eribulin mesylate
Digoxin Immune Fab
Sucralfate
Dorzolamide
Pravastatin
Temsirolimus
naproxen
Memantine
propranolol
Berotralstat
Ursodeoxycholic acid
tamoxifen citrate
atropine sulfate
metoprolol
carbamazepine
ruxolitinib
Corticosteroids
Melphalan
mycophenolate mofetil
Fludarabine
Sodium Phenylbutyrate
etanercept
Denosumab
dapsone
Tofacitinib
mavacamten
minoxidil
ibuprofen
gabapentin
Hydroxychloroquine
cyclophosphamide
bosentan
bimatoprost
testosterone
Artificial tears
Rho(D) immune globulin
Baclofen
Vigabatrin
Clobazam
C1 esterase inhibitor (human)
phacoemulsification surgery
melatonin
amiodarone
Total Parenteral Nutrition
Growth hormone (somatropin)
ascorbic acid
hormone replacement therapy (estrogen/progesterone)
Digoxin
Vitamin B12 (Cobalamin)
Romidepsin
Crizotinib
physical therapy and orthotic management
Retinoids (Tretinoin)
eculizumab
miglustat
tizanidine
Octreotide
aspirin
oxybutynin
Valproic Acid
tocilizumab
sclerostin antibody
Immunoglobulin
Mesalamine
alpha-L-iduronidase
L-DOPA
Intravenous Immunoglobulin (IVIG)
Phenytoin
Bisphosphonates (pamidronate)
Metronidazole
Nitisinone
Human Chorionic Gonadotropin (hCG)
Lomitapide
treprostinil
sirolimus
temozolomide
Carnitine
brivaracetam
Pembrolizumab
Infliximab
folic acid
Pyridoxine
Acetazolamide
Clomiphene Citrate
Angiotensin-Converting Enzyme Inhibitors (Enalapril)
Multivitamin with Calcium and Vitamin D
levothyroxine sodium
ivermectin
botulinum toxin type A
Levothyroxine
azathioprine
sunscreen (broad spectrum SPF 50+)
Somatropin
ambrisentan
Brentuximab vedotin
L-carnitine
insulin
luspatercept
trabectedin
prednisolone
vosoritide
rituximab
Dapagliflozin
allopurinol
Carboplatin
Topical corticosteroids
estradiol
Erythromycin
Erythropoietin
Doxycycline
calcium carbonate
coenzyme Q10
Patisiran
Tolvaptan
cerliponase alfa
adalimumab
Imiglucerase
Amphotericin B liposomal
ranibizumab
Midostaurin
metformin
Methotrexate
carglumic acid
Alendronate Sodium
calcitriol
doxorubicin
Pyridostigmine
Levetiracetam
Cenegermin
Acitretin
prednisone
salicylic acid
Insulin glargine
cochlear implant
Pyridostigmine Bromide
aflibercept
Ravulizumab
laronidase
Romiplostim
Bleomycin
hydroxycobalamin
Laser photocoagulation therapy
acetaminophen
pregabalin
riboflavin
N-acetylcysteine
NovoSeven
Occupational and Physical Therapy Support
eptinezumab
Pamidronate
nitroglycerin
ezetimibe
atorvastatin
bevacizumab
proton pump inhibitors (omeprazole)
Ketoconazole
mecasermin
celecoxib
Biotin
Imiquimod
cyclosporine ophthalmic
Growth Hormone
deferasirox
Tafamidis
urea
Levodopa/Carbidopa
Lanreotide
cyanocobalamin
Sodium Bicarbonate
diazoxide
baricitinib
Azacitidine
Cystagon
Bezafibrate
Zoledronic Acid
Hypertonic saline
copper histidinate
Clonazepam
Zidovudine
emollients with keratolytics
warfarin
Vitamin K1 (Phytonadione)
cornstarch
disopyramide
Sunitinib
Cisplatin
Calcipotriol
Imatinib
imatinib mesylate
nimodipine
Colchicine
Follitropin alfa
surgical repair
Tamoxifen
Tacrolimus
Artificial tears (Hypromellose)
Ribavirin
vitamin D3
Sildenafil
sotalol
Hematopoietic stem cell transplantation
Tretinoin
Diazepam
Timolol maleate
Amnioreduction
AU
Australia
ISO CodeAU
RegionOceania
Regulatory AuthorityTGA (Therapeutic Goods Administration)
Pathways2 documented
Drugs Available210 drug(s)