mannose

Orphan DrugInvestigational

Description

D-mannose is a simple sugar being investigated as a therapeutic substrate for congenital disorders of glycosylation (CDG), including ALG1-CDG. Oral mannose supplementation may bypass certain enzymatic defects in the N-glycosylation pathway and improve protein glycosylation. Clinical trials have shown potential benefit in some CDG subtypes with improvements in biochemical markers and clinical symptoms.

Indications & Therapeutic Use

Congenital disorders of glycosylation (ALG1-CDG, PMM2-CDG)

Linked Diseases:

Global Availability (6 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
mannose
Generic Namemannose
Active IngredientD-mannose
Drug ClassCongenital disorders of glycosylation (ALG1-CDG
ManufacturerVarious
Dosage FormsOral powder for solution; Oral capsule 500mg
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Lead Time14 days
Reg. StatusInvestigational
Clinical TrialNCT02870426
Countries6 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations7 Validated Nodes