Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
OrphanDrug
OrphanDrug
Pharma Knowledge Base
DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs

Navigation

DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs

About

OrphanDrug covers global rare drug access intelligence for 193 countries.

HomeDrugs

Drug Database

13 entries
Clear
AllABCDEFGHIJKLMNOPQRSTUVWXYZ
Orphan Drugs Only
Acitretin
Orphan3dFDA Approved
alglucosidase alfa
Orphan Cold Chain7dFDA Approved, EMA Approved
alpha-L-iduronidase
Orphan Cold Chain14dFDA Approved, EMA Approved
ambrisentan
Orphan10dFDA Approved
Amnioreduction
OrphanStandard of care
Amphotericin B liposomal
Orphan Cold Chain5dFDA Approved, EMA Approved
Anakinra
Orphan Cold Chain14dFDA Approved
Arsenic trioxide
OrphanFDA Approved
asciminib
Orphan7dFDA Approved, EMA Approved
Ataluren
Orphan21dEMA Approved
atidarsagene autotemcel
Orphan Cold Chain90dEMA Approved
avalglucosidase alfa
Orphan Cold Chain21dFDA Approved (2021), EMA Approved (2021)
Azacitidine
Orphan Cold Chain5dFDA Approved
OrphanDrug — Global Pharma Knowledge Base
DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs|Terms of UsePrivacy Policy