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Drugs Diseases Countries Pathways Programs Suppliers API Docs

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OrphanDrug covers global rare drug access intelligence for 193 countries.

HomeDrugs

Orphan & Rare Drug Database

15 entries

All A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Orphan Drugs Only

Orphan3dFDA Approved

OrphanFDA Approved (2024)

alglucosidase alfa

Orphan Cold Chain7dFDA Approved, EMA Approved

alpha-L-iduronidase

Orphan Cold Chain14dFDA Approved, EMA Approved

Orphan10dFDA Approved

OrphanStandard of care

Amphotericin B liposomal

Orphan Cold Chain5dFDA Approved, EMA Approved

Orphan Cold Chain14dFDA Approved

Arsenic trioxide

OrphanFDA Approved

Orphan7dFDA Approved, EMA Approved

Orphan21dEMA Approved

atidarsagene autotemcel

Orphan Cold Chain90dEMA Approved

avalglucosidase alfa

Orphan Cold Chain21dFDA Approved (2021), EMA Approved (2021)

Orphan Cold ChainFDA Approved (2024)

Orphan Cold Chain5dFDA Approved

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