Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan Drugs Only
L-carnitine
Orphan
5d
FDA Approved, EMA Approved
Lanreotide
Orphan
Cold Chain
14d
FDA Approved
laronidase
Orphan
Cold Chain
14d
FDA Approved, EMA Approved
Laser photocoagulation therapy
Orphan
FDA Approved
Lomitapide
Orphan
FDA Approved
lonafarnib
Orphan
21d
FDA Approved, EMA Approved
loncastuximab tesirine
Orphan
Cold Chain
14d
FDA Approved (2021), EMA Approved (2022)
Lumasiran
Orphan
Cold Chain
FDA Approved, EMA Approved
luspatercept
Orphan
Cold Chain
10d
FDA Approved, EMA Approved