Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
OrphanDrug
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

9 entries
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Orphan Drugs Only
L-carnitine
Orphan5dFDA Approved, EMA Approved
Lanreotide
Orphan Cold Chain14dFDA Approved
laronidase
Orphan Cold Chain14dFDA Approved, EMA Approved
Laser photocoagulation therapy
OrphanFDA Approved
Lomitapide
OrphanFDA Approved
lonafarnib
Orphan21dFDA Approved, EMA Approved
loncastuximab tesirine
Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022)
Lumasiran
Orphan Cold ChainFDA Approved, EMA Approved
luspatercept
Orphan Cold Chain10dFDA Approved, EMA Approved
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