Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
OrphanDrug
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

4 entries
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Orphan Drugs Only
Vigabatrin
Orphan14dFDA Approved, EMA Approved
Vorasidenib
Orphan14dFDA Approved
vosoritide
Orphan Cold Chain21dFDA Approved
vutrisiran
Orphan Cold Chain18dFDA Approved (2022), EMA Approved (2022)
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