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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

126 entries
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Orphan Drugs Only
Cisplatin
Orphan7dFDA Approved
Clobazam
OrphanFDA Approved
copper histidinate
Orphan Cold Chain14dFDA Approved (Orphan)
Corticotropin
Orphan Cold ChainFDA Approved
Crizanlizumab
Orphan Cold Chain14dFDA Approved
Crizotinib
Orphan10dFDA Approved
cyclosporine ophthalmic
Orphan5dFDA Approved
Cystagon
OrphanFDA Approved
cysteamine bitartrate
Orphan Cold Chain14dFDA Approved
Dabrafenib
OrphanFDA Approved
deferasirox
Orphan5dFDA Approved, EMA Approved
Deflazacort
Orphan7dFDA Approved
Dexrazoxane
Orphan7dFDA Approved
diazoxide
Orphan14dFDA Approved, EMA Approved
Digoxin Immune Fab
Orphan Cold Chain7dFDA Approved
eculizumab
Orphan Cold Chain14dFDA Approved, EMA Approved
Edaravone
Orphan7dFDA Approved
efgartigimod alfa
Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022), Japan Approved (2022)
eladocagene exuparvovec
Orphan Cold Chain45dEMA Approved (2022)
eliglustat
Orphan10dFDA Approved, EMA Approved
eplontersen
Orphan Cold Chain21dFDA Approved (2023), EMA Approved (2024)
Epoprostenol
Orphan Cold Chain14dFDA Approved
eribulin mesylate
Orphan Cold Chain14dFDA Approved
Erythropoietin
Orphan Cold Chain14dFDA Approved
Eteplirsen
Orphan Cold ChainFDA Approved
Everolimus
OrphanFDA Approved
Fludarabine
Orphan Cold Chain10dFDA Approved
fosdenopterin
Orphan Cold Chain30dFDA Approved (2021), Unregistered in India
GM-CSF
Orphan Cold ChainFDA Approved
Growth hormone (somatropin)
Orphan Cold Chain14dFDA Approved
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