Imiglucerase

Orphan Drug Cold Chain RequiredFDA Approved

Description

Imiglucerase is a recombinant DNA-derived form of the human enzyme acid beta-glucosidase. It is used as enzyme replacement therapy for patients with Gaucher disease.

Indications & Therapeutic Use

Gaucher's disease type I, Gaucher's disease type III

Linked Diseases:

Gaucher Disease
E75.22D005776

Evidence: Multiple RCTs, standard of care

Global Availability (6 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus
Registered5 daysCommercially available

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Imiglucerase
Generic NameImiglucerase
Brands1 brand available
Active IngredientImiglucerase
Drug ClassGaucher's disease type I
ManufacturerSanofi Genzyme
Dosage FormsIV infusion, 200 units/vial, 400 units/vial
Medical CodeA16AB02
Orphan StatusYes — Orphan Drug
Cold ChainRequired
Lead Time14 days
Reg. StatusFDA Approved
Countries6 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations7 Validated Nodes