IN

India

IN

South Asia

Regulatory Overview

India is regulated by the CDSCO. The country has 3 documented regulatory pathways for accessing unapproved or unlicensed medicines, covering named patient programs, compassionate use schemes, and special access arrangements.

Regulatory Authority

CDSCO

Regulatory Pathways (3)

Rule 96 of NDCT Rules 2019 allows compassionate use of new drugs for patients with serious or life-threatening diseases who are not eligible for clinical trials and have no other treatment options.

Application Form: CDSCO CU Application
Legal Basis: NDCT Rules 2019 Rule 96
Eligibility: Serious or life-threatening condition with no locally registered alternative
Reference: CDSCO New Drugs and Clinical Trials Rules 2019

Under India's New Drugs and Clinical Trials Rules 2019, a named patient can import unapproved drugs on Form 12B with CDSCO approval for personal use to treat a specific disease.

Application Form: Form 12B
Legal Basis: NDCT Rules 2019, Rule 101
Eligibility: Serious or life-threatening condition with no locally registered alternative
Reference: CDSCO GSR 354(E) 2019

Under India's New Drugs and Clinical Trials Rules 2019, a named patient can import unapproved drugs...

Application Form: Form 12B
Legal Basis: Regulated
Eligibility: Patient must have no alternative licensed treatment available in India.
Reference: CDSCO GSR 354(E)

Drugs Available (84)

DrugAccess RouteStatusLead Time
cytarabine
furosemide
Sucralfate
propranolol
tamoxifen citrate
atropine sulfate
metoprolol
carbamazepine
mycophenolate mofetil
diethylcarbamazine
minoxidil
ibuprofen
gabapentin
Artificial tears
Baclofen
phacoemulsification surgery
ascorbic acid
Digoxin
physical therapy and orthotic management
aspirin
oxybutynin
Valproic Acid
Immunoglobulin
Phenytoin
Metronidazole
sirolimus
temozolomide
folic acid
Pyridoxine
Acetazolamide
Angiotensin-Converting Enzyme Inhibitors (Enalapril)
Multivitamin with Calcium and Vitamin D
levothyroxine sodium
ivermectin
azathioprine
sunscreen (broad spectrum SPF 50+)
L-carnitine
insulin
prednisolone
rituximab
allopurinol
Topical corticosteroids
Erythromycin
Doxycycline
calcium carbonate
coenzyme Q10
tacrolimus ophthalmic
ImigluceraseRegisteredCommercially available5 days
metformin
diacerein
Methotrexate
calcitriol
doxorubicin
Pyridostigmine
Levetiracetam
prednisone
salicylic acid
Insulin glargine
cochlear implant
Pyridostigmine Bromide
Bleomycin
acetaminophen
pregabalin
riboflavin
Diosmin
atorvastatin
bevacizumab
proton pump inhibitors (omeprazole)
Biotin
deferasirox
RisdiplamNamed PatientAvailable via NPP7 days
urea
Levodopa/Carbidopa
cyanocobalamin
Hypertonic saline
emollients with keratolytics
surgical repair
Tamoxifen
Artificial tears (Hypromellose)
vitamin D3
NusinersenNamed PatientAvailable via NPP7 days
Hematopoietic stem cell transplantation
Timolol maleate
Amnioreduction
IN
India
ISO CodeIN
RegionSouth Asia
Regulatory AuthorityCDSCO
Pathways3 documented
Drugs Available84 drug(s)