Methotrexate

Orphan DrugFDA Approved

Description

Methotrexate is an antimetabolite and antifolate drug used in the treatment of gestational trophoblastic neoplasms including choriocarcinoma and hydatidiform mole. It inhibits dihydrofolate reductase, preventing DNA synthesis in rapidly dividing cells. Methotrexate has been a cornerstone of treatment for low-risk gestational trophoblastic disease for decades.

Indications & Therapeutic Use

Gestational trophoblastic neoplasm, choriocarcinoma, hydatidiform mole, rheumatoid arthritis, psoriasis

Global Availability (9 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Methotrexate
Generic NameMethotrexate
Brands1 brand available
Active IngredientMethotrexate
Drug ClassGestational trophoblastic neoplasm
ManufacturerMultiple manufacturers
Dosage FormsOral tablet 2.5mg, 5mg, 7.5mg, 10mg, 15mg; Injectable solution 25mg/mL
Medical CodeL01BA01
Orphan StatusYes — Orphan Drug
Cold ChainNot Required
Lead Time3 days
Reg. StatusFDA Approved
Clinical TrialNCT00339235
Countries9 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations10 Validated Nodes