Pyridoxine

FDA Approved

Description

Pyridoxine (Vitamin B6) is used in the treatment of hereditary sideroblastic anemia, particularly X-linked sideroblastic anemia caused by ALAS2 mutations. It acts as a cofactor for delta-aminolevulinic acid synthase, the first enzyme in heme biosynthesis. Some patients with hereditary sideroblastic anemia respond to high-dose pyridoxine supplementation with improved hemoglobin levels.

Indications & Therapeutic Use

Hereditary sideroblastic anemia, pyridoxine-responsive anemia, vitamin B6 deficiency

Linked Diseases:

Global Availability (8 countries)

CountryAccess RouteRegulatory PathwayLead TimeStatus

Available Through

This drug is available for procurement through the following fulfilment partner.

Fulfilment Partner
Pyridoxine
Generic NamePyridoxine
Active IngredientPyridoxine hydrochloride
Drug ClassHereditary sideroblastic anemia
ManufacturerVarious
Dosage FormsOral tablets 25mg, 50mg, 100mg; Injectable solution 100mg/mL
Medical CodeA11HA02
Orphan StatusNo
Cold ChainNot Required
Lead Time7 days
Reg. StatusFDA Approved
Countries8 countries
Authority Signals
Last Verified3/21/2026
Data ConfidenceHigh (AI + Pharmacist)
Source Citations9 Validated Nodes