Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan Drugs Only
Tafamidis
Orphan
10d
FDA Approved
temozolomide
Orphan
7d
FDA Approved, EMA Approved
Temsirolimus
Orphan
Cold Chain
FDA Approved
Tolvaptan
Orphan
14d
FDA Approved
trabectedin
Orphan
Cold Chain
21d
FDA Approved
Trametinib
Orphan
FDA Approved
treprostinil
Orphan
14d
FDA Approved
triheptanoin
Orphan
21d
FDA Approved, EMA Approved