Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

21 entries
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Orphan Drugs Only
Baclofen
7dFDA Approved
baricitinib
Orphan14dFDA Approved, EMA Approved
belumosudil
Orphan10dFDA Approved
Belzutifan
Orphan14dFDA Approved
Beremagene geperpavec
Orphan Cold Chain14dFDA Approved
Berotralstat
Orphan14dFDA Approved
Betaine anhydrous
Orphan21dFDA Approved
bevacizumab
Cold Chain14dFDA Approved, EMA Approved
Bezafibrate
Approved
bimatoprost
14dFDA Approved
Bimekizumab-bkzx
Cold Chain7dFDA Approved
Biotin
3dFDA Approved (as supplement)
Bisphosphonates (pamidronate)
10dFDA Approved
Bleomycin
Cold Chain7dFDA Approved, EMA Approved
bosentan
Orphan10dFDA Approved
botulinum toxin type A
Cold Chain14dFDA Approved
Botulism Antitoxin Heptavalent (A, B, C, D, E, F, G) - (Equine)
Orphan Cold Chain2dFDA Approved
Branched-Chain Amino Acids
Brentuximab vedotin
Orphan Cold Chain7dFDA Approved
brivaracetam
Orphan10dFDA Approved
Busulfan
Orphan14dFDA Approved
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